A Blinded, Placebo-Controlled Systemic Gene Therapy Efficacy Study in the GRMD Model of Duchenne Muscular Dystrophy Conference Paper uri icon

published proceedings

  • MOLECULAR THERAPY

author list (cited authors)

  • Birch, S. M., Lawlor, M. W., Guo, L., Crudele, J. M., Hawkins, E. C., Nghiem, P. P., ... Kornegay, J. N.

complete list of authors

  • Birch, Sharla M||Lawlor, Michael W||Guo, Lee-Jae||Crudele, Julie M||Hawkins, Eleanor C||Nghiem, Peter P||Styner, Martin A||Struharik, Michael J||Brown, Kristy J||Golebiowski, Diane||Gonzalez, J Patrick||Morris, Carl A||Schneider, Joel S||Chamberlain, Jeffrey S||Byrne, Barry J||Kornegay, Joe N

publication date

  • January 2017